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· 제목 : Genome Editing: The Next Step in Gene Therapy (Hardcover, 2016) 
· 분류 : 외국도서 > 의학 > 유전학
· ISBN : 9781493935079
· 쪽수 : 263쪽
· 출판일 : 2016-03-05
· 분류 : 외국도서 > 의학 > 유전학
· ISBN : 9781493935079
· 쪽수 : 263쪽
· 출판일 : 2016-03-05
목차
1. Gene Editing: Double-Strand Break Induced Gene Targeting and Mutagenesis 20 Years Later.- 2. The Development and Use of Zinc-Finger Nucleases.- 3.The Use and Development of TAL Effector Nucleases.- 4. Genome Editing for Neuromuscular Diseases.- 5. Phage Integrases for Genome Editing.- 6. Precise Genome Modification Using Triplex Forming Oligonucleotides and Peptide Nucleic Acids.- 7. Genome Editing by Aptamer-Guided Gene Targeting.- 8. Stimulation of AAV Gene Editing via DSB Repair.- 9. Engineered Nucleases and Trinucleotide Repeat Diseases.- 10. Using Engineered Nucleases to Create HIV-Resistant Cells.- 11. Strategies to Determine Off-Target Effects of Engineered Nucleases.
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